SMA newborn screening programs were available in 31 countries in 2023, covering about 7% of the world's newborns, per a study.
A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...
A study found profound swallowing deficits in SMA type 1 babies, a disease feature of note as disease-modifying treatment ...
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