Meet our experts who are among the world's leaders in treating retina-related disorders and conditions, such as macular degeneration, diabetic retinopathy, retinal detachment, vein occlusion and ...
Presa, Bailey et al. assess the feasibility and efficacy of intrathecal administration of AAV9-SUMF1 gene therapy in the Sumf1-KO mouse model of Multiple Sulfatase Deficiency. They show that it ...