Jaden Lim hopes to raise awareness of spinal muscular atrophy and get sponsors to donate RM10 per km of his climb for his brother.

Study using a new, child-friendly scale found patients up to age 2 had smaller mouth openings than healthy peers, risking ...

Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.

CAMBRIDGE, Mass. - Scholar Rock (NASDAQ: SRRK), a biopharmaceutical company with a market capitalization of $3.96 billion and an impressive 362.73% stock price surge over the past six months, ...

Z526- a novel dithiocarbamate-like compound reverses cancer associated cachexia via mitigating NF-B signaling and oxidative ...

A monthly 10 mg/mL maintenance dose of Leqembi had the same effects on mild Alzheimer’s symptoms as biweekly dose, research ...

One-year-old Asmika Das from Ranaghat, Nadia, is suffering from a fatal disease called Spinal Muscular atrophy.

Roche has reported positive results from the second year of the EMBARK Phase III trial of Elevidys (delandistrogene moxeparvovec), the first approv ...

Muscular dystrophy (MD) represents a group of inherited muscle disorders that primarily cause muscle weakness and muscle wasting, though some types of the disease also present with other ...

Applications are based on data from the DEVOTE study, which demonstrate the potential for the investigational higher dose regimen of nusinersen to advance the treatment of SMA CAMBRIDGE, Mass., Jan. 2 ...

SPINRAZA is an approved treatment for spinal muscular atrophy in over 71 countries ... full results or results from later stage or larger scale clinical trials and do not ensure regulatory ...

The following is a summary of “Spinal cord gray matter atrophy is associated with disability in spinal muscular atrophy,” published in the January 2025 issue of Neurology by Kesenheimer et al. With ...