Scientists have identified novel genetic interactions that may contribute to congenital heart disease (CHD), a common birth defect. Scientists at the Icahn School of Medicine at Mount Sinai and ...

To mark progress on rare diseases, experts across the country, including those at @HopkinsMedicine, will celebrate #RareDiseaseDay on Feb. 28. › Click to Tweet As key members of the Johns Hopkins ...

Doctors harvest stem cells from the patient’s bone marrow and then send them off to a lab, where CRISPR is used to turn up the production of another, functional version of haemoglobin. This version is ...

Like recombinant DNA before it, gene editing has the potential to transform medicine, agriculture and more. CRISPR is now used by thousands of biologists in labs across the globe. A revolution in food ...

Aug. 29, 2024 — For decades, scientists have dreamt of a future where genetic diseases, such as the blood clotting disorder hemophilia, could be a thing of the past. Gene therapy, the idea of ...

A two-and-a-half-year-old girl shows no signs of a rare genetic disorder ... Babies with severe disease don’t usually live past their third birthday. In the past decade, the US Food and Drug ...

it often means both parents unknowingly carried genetic variations that, when combined, led to the disease. Modern genetic testing now allows families to understand their risk factors better ...

The global viral vector and plasmid DNA manufacturing market size is calculated at USD 8.66 billion in 2025 and is expected ...

Berlin, Germany, and Research Triangle Park, N.C., USA, Feb. 19, 2025 (GLOBE NEWSWIRE) -- Not intended for UK Media Regenerative Medicine Advanced Therapy (RMAT) designation follows Phase Ib 36-month ...

Experts from Oxford University examined the impact of 164 environmental factors and genetic risks for 22 major diseases in ...

Discover the first in-utero treatment for spinal muscular atrophy (SMA) using risdiplam. Promising results show no SMA signs ...