Research led by Children's Hospital of Fudan University in China has found that a gene called pancreatic progenitor cell ...

Researchers can experimentally interrogate the function of one or more genes using knockout or knockdown tools. Although both approaches ultimately interfere with gene function, knockout and knockdown ...

Single IV administration of tau silencing gene therapy VY1706 significantly reduced tau mRNA and protein levels, with broad ...

1 Scientists have harnessed RNAi in the laboratory to selectively silence target gene expression, a technique known as gene knockdown. 8 By delivering dsRNA that are complementary to a target gene’s ...

Voyager Therapeutics (VYGR) reported new data from its two preclinical programs targeting tau for the treatment of Alzheimer’s disease. Data on ...

Single IV administration of tau silencing gene therapy VY1706 significantly reduced tau mRNA and protein levels, with broad brain distribution and liver de-targeting, in NHP study - - Preclinical muri ...

Last year, Penn Medicine did the first successful external liver perfusion using a gene-edited pig liver. Blood in a brain-dead patient circulated through a pig’s liver that was outside the ...