Rolling Out11 小时
5 ways AI and love conquered a deadly blood disorder
Machine learning and unwavering support helped Joseph Coates overcome POEMS syndrome. Discover how computational medicine is ...
US FDA greenlights first-ever treatment for rare genetic disorder
The U.S. Food and Drug Administration approved Soleno Therapeutics' drug to treat a rare genetic disorder on Wednesday, ...
Dallas scientists granted $420K to test gene therapy for rare neurological disease
Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...
Healio17 小时
Patients with COPD plus depression or anxiety experience greater disease burden
Patients with COPD plus a depression/anxiety disorder had poorer scores related to disease burden and health-related quality of life, according to data published in Chronic Obstructive Pulmonary ...
BioPharma Dive16 小时
Epicrispr banks $68M to test epigenetic editing on rare muscle disease
The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...
The New England Journal of Medicine8 小时
Beyond Glucocorticoids for IgG4-Related Disease
IgG4-related disease is an increasingly recognized fibroinflammatory condition with protean manifestations. The disorder is ...
Citizen Digital26 分钟
US FDA approves first treatment for rare genetic disorder Prader-Willi syndrome
The U.S. Food and Drug Administration on Wednesday approved Soleno Therapeutics' (SLNO.O) drug to treat a rare genetic ...
Johns Hopkins Medicine3 天
Scientists Identify Potential New Genetic Target for Sickle Cell Disease Treatment
Scientists from Johns Hopkins Medicine and eight other institutions in the United States, Africa and Europe say they have ...
News-Medical.Net on MSN1 天
Oklahoma researcher uses technology to combat alcohol use disorder in primary care
According to the Centers for Disease Control and Prevention, 1 in 7 adults in the United States will experience a substance use disorder during their lifetime. University of Oklahoma College of ...
Couple with Brittle Bone Disease Says It’s ‘Taxing’ but ‘Disability Isn't Something ...
In an exclusive interview with PEOPLE, Jay and Pamela — both born with osteogenesis imperfecta, or brittle bone disease — ...
Japan Today8 小时
Poor sleep linked to advanced stages of a complex heart and kidney disease syndrome
People with a complex heart, kidney and metabolic-related condition who got better quality sleep were less likely to have an advanced stage of the illness than those getting poor sleep, according to a ...