Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...

"Acadia submits MAA to EMA for Rett syndrome therapy" was originally created and published by Pharmaceutical Technology, a ...

Rett syndrome predominantly affects girls, with symptoms typically emerging after an initial period of normal development. Children with Rett syndrome often appear healthy in the first 6 to 18 months, ...

aimed at treating Rett syndrome in adults and in children aged two years and older. This rare genetic neurological and developmental disorder impacts brain development and affects mainly females.

It's not easy to deal with tragedy, but for Colin Endres and the D-Y/CCT/CCA boys hockey team, they're honoring his sister ...

Rizzo is diagnosed with Rett syndrome, which leads to a regression of basic skills that a small child may have already learned. Her parents say that the volunteers at Sebastian Riding Associates ...

(Nasdaq: ACAD) today announced that the company has submitted a Marketing Authorization Application (MAA) to the European Medicines Agency (EMA) for trofinetide for the treatment of Rett syndrome ...

2-4 A child with Rett syndrome exhibits an early period of apparently normal development until six to 18 months, when their skills seem to slow down or stagnate. This is typically followed by a ...

Survivors include his wife of over 30 years, Marilyn Zawada Rett; children Donald Anthoney Rett (Laura); Jennifer T. Rett; Jonathan M. Rett (Colleen); Juliana Johnson; Bradley Yeomans; and ...