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Gene Therapy May Be a Game Changer for Transfusion-Dependent Thalassemia
The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...
Sickle cell disease is a genetic disorder that causes lifelong suffering – here’s what you need to know
Accumulation of clots causes some of the most severe symptoms of sickle cell disease, including strokes, kidney failure, ...
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After a no in sickle cell, NICE OKs Casgevy for thalassaemia
It involves harvesting bone marrow stem cells from patients ... transfusion-dependent beta thalassaemia, freeing them from the burden and risks of needing regular blood transfusions," said the ...
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Thalassemia and Pregnancy: What Every Expecting Parent Needs to Know
Thalassemia remains a pressing health issue in India, with the country bearing a significant burden of this hereditary disorder. Despite advancements in treatment, the condition continues to ...
IRCS-Mancherial blood bank turns boon for thalassemia, sickle cell patients
The patients belonging to not only from erstwhile Adilabad, Warangal, Karimnagar districts, but also from Sironcha of ...
Leukofilter bag crisis in VIMSAR, patients suffer in Odisha
SAMBALPUR: The acute shortage of leukofilter bags at Veer Surendra Sai Institute of Medical Sciences and Research (VIMSAR), ...
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Beti-cel gene therapy achieves high rates of transfusion independence in severe β-thalassemia
There were no serious adverse events or treatment-related mortalities. Evidence Rating Level: 2 (Good) Study Rundown: ...