资讯

Purpose: X-linked infantile spinal-muscular atrophy (XL-SMA) is a rare disorder, which presents with the clinical characteristics of hypotonia, areflexia, and multiple congenital contractures ...
Veteran actor Eric Dane shared that he was diagnosed with amyotrophic lateral sclerosis (ALS), a rare degenerative disease ...
for apitegromab for the improvement of motor functions in patients with spinal muscular atrophy (SMA). Apitegromab, a fully human monoclonal antibody, works by selectively binding to the pro- and ...
Supreme Court examines pleas challenging 50 lakh cap on Centre's assistance for treating rare diseases like SMA.
A UConn professor and researcher who 28 years ago discovered a gene for a protein that limits human muscle growth is closer than ever to having that work play a significant role in treating those with ...
The bench said that public good outweighs the company’s profit as the drug is not available at an affordable price in India.
Apitegromab, a fully human monoclonal antibody, works by selectively binding to the pro- and latent forms of myostatin in order to inhibit myostatin activation.
ISLAMABAD: A five-year plan to eradicate spinal muscular atrophy (SMA), a genetic disorder causing progressive muscle weakness that was once a leading cause of infant mortality has been launched.
Novartis has announced positive results from a late-stage programme of its experimental gene replacement therapy in patients with the rare neuromuscular disease spinal muscular atrophy (SMA). The ...
In a proof-of-concept study involving five individuals with spinal cord injuries, the combination of robotics and electrical epidural stimulation resulted in immediate and sustained muscle activation.