This previously untreatable genetic disorder, which affects some two to three of every 10 million newborn babies, leads to profound visual impairments and legal blindness. In turn, this causes ...

Is your eye twitching a sign of stress or something serious Explore the causes from lifestyle factors to neurological ...

Rare eye diseases are the leading cause of untreatable ... An intensive therapy for children with neuromotor disorders developed by Virginia Tech researchers shows promise for kids with a rare ...

Alnylam has said it will not proceed with a clinical trial of its RNAi drug vutrisiran in the rare eye disorder Stargardt disease – at least for now – tying its decision to President Joe Biden ...

March 7, 2025 – The FDA has approved a new gene therapy for macular telangiectasia type 2 (MacTel), a rare eye disease that causes vision loss. The approval marks the first and only ...

Neurotech Pharma's cell therapy Encelto has become the first FDA-approved treatment for idiopathic macular telangiectasia type 2 (MacTel), a rare eye disease leading to progressive and ...