For those living with sickle cell disease, daily life is a series of obstacles that demand unwavering strength. The condition is relentless, marked by excruciating pain crises, organ damage ...
Would it be a cure for my sickle cell disease? It was a decision I could think about making because my sister was a genetic match and could donate her stem cells. Most with sickle cell don’t ...
Brains of people with sickle cell disease appear older Study also finds socioeconomic status linked to brain health in adults Date: January 17, 2025 Source: WashU Medicine Summary: A new study has ...
Gallbladder problems are a common complication in individuals with sickle cell disease. These issues often arise due to the breakdown of red blood cells and the subsequent formation of gallstones ...
Given the remarkable advances seen with gene therapies for sickle cell disease (SCD), it may seem counterintuitive to suggest the space may be in need of more therapies that have already been ...
However, carriers can have children who inherit sickle cell disease and may exhibit symptoms. Therefore, unless you conduct DNA paternity tests that confirm the child is not yours, the fact that ...
A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...
Our independent appraisal committee has approved the use of gene editing therapy exagamglogene autotemcel (exa-cel) for use in the NHS in England, providing a potential cure for some people with ...
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also known as exa-cel, was the first treatment to be licensed using gene ...