With its recent data drop for an oligonucleotide candidate, Dyne Therapeutics signals it may become a frontrunner in this ...
An alteration in the causative gene, dystrophia myotonica protein kinase (DMPK), leads to a toxic messenger RNA (mRNA) that participates in the sequestration of muscleblind-like (MBNL) proteins ...
Claudio [email protected] Biological Sciences Target Discovery & Characterization Cancer, Neurological Disorder/Trauma Altman, Ryan [email protected] Medicinal Chem/Molecular Pharmacology Drug ...