Orphan drugs offer critical treatment options for rare diseases, improving quality of life for underserved patients and ...

By Daniella Parra March Biosciences was granted an orphan drug designation from the FDA to MB-105, its CD5-targeted CAR-T ...

MB-105, a first-in-class CD5-targeted CAR T-cell therapy, received FDA orphan drug designation for relapsed/refractory T-cell ...

While the former Biden administration showcased the Inflation Reduction Act as a key victory in the fight over high drug ...

据公开信息，该候选药物拟治疗的适应症是被称为全球五大绝症之首的运动神经元疾病——渐冻症，渐冻症又名肌萎缩侧索硬化症（ALS），著名社会活动“冰桶挑战”源于渐冻症绝症患者的家庭和支持者。 此前，士泽生物另一款人异体通用“现货型”中脑多巴胺能神经前体细胞注射液（“XS-411注射液”）IND 申请获得国家药监局受理。据了解，该候选药物的适应症是 帕金森病 。

Biosciences receives US FDA orphan drug designation for MB-105 to treat relapsed/refractory CD5-positive T-cell lymphoma: Houston Thursday, January 30, 2025, 17:00 Hrs [IST] ...

Zydus has announced that the USFDA has granted Orphan Drug Designation (ODD) to Usnoflast, a novel oral NLRP3 inhibitor, for ...

Orphan Drugs Market Orphan Drugs Market Dublin, Jan. 22, 2025 (GLOBE NEWSWIRE) -- The "Orphan Drugs - Global Strategic ...

KalVista Pharmaceuticals, Inc. (NASDAQ: KALV), today announced that Japan’s Ministry of Health, Labour and Welfare (MHLW) has ...

Zydus Lifesciences's Usnoflast receives Orphan Drug Designation from the USFDA for the treatment of Amyotrophic Lateral ...

Zydus Lifesciences announced that the USFDA granted Orphan Drug Designation to Usnoflast, a novel oral NLRP3 inhibitor, for ...

Seed Therapeutics Inc.’s ST-01156 has been awarded orphan drug designation for the treatment of Ewing sarcoma as well as rare pediatric disease designation by the FDA.